News & Events

• September 23, 2017
  

  Seeking a Better Landscape for Therapy Development in Neuromuscular Disorders

  Larkindale J, Porter JD. Seeking a Better Landscape for Therapy Development in Neuromuscular Disorders. Issues & Opinions: Improved Data Sharing for NMDs. Muscle & Nerve. 2017 Sep 23.

• July 28, 2017
  

  Dopamine transporter neuroimaging as an enrichment biomarker in early Parkinson’s disease clinical trials: a disease progression modeling analysis

  Conrado DJ, Nicholas T, Tsai K, Macha S, Sinha V, Stone J, Corrigan B, Bani M, Muglia P, Watson IA, Kern VD, Sheveleva E, Marek K, Stephenson DT, Romero K, on behalf of the Critical Path for Parkinson’s (CPP) Parkinson’s Disease Modeling and Simulation Working Group. Dopamine Transporter Neuroimaging as an Enrichment Biomarker in Early Parkinson’s Disease Clinical Trials: A Disease Progression Modeling Analysis: Dopamine Transporter Imaging Enrichment Biomarker. Clinical and Translational Science. 2017 Jul 27.

• July 4, 2017
  

  Open Innovation: Towards Sharing of Data, Models and Workflows

  Conrado DJ, Karlsson MO, Romero K, Sarr C, Wilkins JJ. Open Innovation: Towards Sharing of Data, Models and Workflows. European Journal of Pharmaceutical Sciences: Official Journal of the European Federation for Pharmaceutical Sciences. 2017 Jul 4.

• June 12, 2017
  

  Regulatory Science in Neonates: A Framework That Supports Evidence-Based Drug Therapy

  Turner MA, Portman RJ, Davis JM. Regulatory Science in Neonates: A Framework That Supports Evidence-Based Drug Therapy. JAMA pediatrics. 2017 Jun 12.

   

• May 31, 2017
  

  Development of a Harmonized Patient-Reported Outcome Questionnaire to Assess Myelofibrosis Symptoms in Clinical Trials

  Gwaltney C, Paty J, Kwitkowski VE, Mesa RA, Dueck AC, Papadopoulos EJ, Wang L, Feliciano J, Coons SJ. Development of a Harmonized Patient-Reported Outcome Questionnaire to Assess Myelofibrosis Symptoms in Clinical Trials. Leukemia Research. 2017;59:26–31.