News & Events
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December 1, 2017
Emerging Good Practices for Translatability Assessment (TA) of Patient-Reported Outcome (PRO) Measures
Acquadro C, Patrick D, Eremenco S, Martin M, Kuliś D, Correia H, et al. Emerging good practices for Translatability Assessment (TA) of Patient-Reported Outcome (PRO) measures. Journal of Patient-Reported Outcomes. 2017;(2):8.
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November 24, 2017
Chronic Pulmonary Insufficiency of Prematurity: Developing Optimal Endpoints for Drug Development
Steinhorn R, Davis JM, Göpel W, Jobe A, Abman S, Laughon M, Bancalari E, Aschner J, Ballard R, Greenough A, Storari L, Thomson M, Ariagno RL, Fabbri L, Turner MA. Chronic Pulmonary Insufficiency of Prematurity: Developing Optimal Endpoints for Drug Development. The Journal of Pediatrics. 2017 Dec 1;191:15–21.e1.
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November 22, 2017
What Evidence Do We Need for Biomarker Qualification?
Leptak C, Menetski JP, Wagner JA, Aubrecht J, Brady L, Brumfield M, Chin WW, Hoffmann S, Kelloff G, Lavezzari G, Ranganathan R, Sauer JM, Sistare FD, Zabka T, Wholley D. What Evidence Do We Need for Biomarker Qualification? Science Translational Medicine. 2017 Nov 22;9(417).
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October 26, 2017
226th ENMC International Workshop: Towards Validated and Qualified Biomarkers for Therapy Development for Duchenne Muscular Dystrophy
Aartsma-Rus A, Ferlini A, McNally EM, Spitali P, Sweeney HL, Aartsma-Rus AM, Szigyarto CAK, Bello L, Bronson A, Brown K, Buccella F, Chadwick J, Ferlini A, Frank D, Hoffman E, Larkindale J, McClorey G, McNally E, Munschauer R, Muntoni F, Owens J, Schara U, Spitali P, Straub V, Sweeney L, Tinsley J, Versnel J, Vroom E, Welch E. 226th ENMC International Workshop: Towards Validated and Qualified Biomarkers for Therapy Development for Duchenne Muscular Dystrophy. Neuromuscular Disorders. 2017 Oct.
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October 1, 2017
Enrollment of Neonates in More Than One Clinical Trial
Davis JM, Baer GR, Portman R, Nelson R, Storari L, Aranda JV, Bax R, Zajicek A, Klein A, Turner M, Baygani S, Thomson M, Allegaert K, International Neonatal Consortium. Enrollment of Neonates in More Than One Clinical Trial. Clinical Therapeutics. 2017 Oct;39(10):1959–69.